09th-10th October 2023

4th Annual MarketsandMarkets Orphan Drugs and Rare Diseases Conference

London, UK

The present-day challenges, including constrained resources, disease severity, limited patient access, and a lack of available knowledge in rare diseases, necessitate the discovery of innovative solutions to hasten orphan drug development.

With the enforcement of the 1983 Orphan Drug Act (ODA), manufacturers are obliged to scale production to treat rare/orphan diseases, leading to a drastic advancement in the landscape of orphan drugs. Novel therapies aimed at treating these uncommon diseases are paramount to fulfilling the unmet needs of patients.

The 4th Annual MarketsandMarkets Orphan Drugs and Rare Diseases Conference, to be held on October 9–10 in London, UK, aims to provide a valuable and broad platform to discuss recent advances in the development of life-saving therapies, critical issues, and strategies to enhance orphan drug development in near future. The conference will bring together scientists, researchers, entrepreneurs, academicians, medical officials, and technologists across the globe to discuss the newest findings in the areas of rare diseases and orphan drugs, helping to shape present and upcoming challenges in drug analysis. It gives participants the chance to interact with industry peers and participate in this scientific conference while staying informed about the most recent developments in the study of rare diseases.


Key Highlights

  • Current landscape of Orphan Drugs across the globe.
  • Next Generation therapies treating uncommon/rare infections.
  • Practices to enhance access to patient data.
  • Clinical development & regulatory.
  • Digital health and Artificial intelligence.
  • Existing roadblocks in orphan drug development.
  • Pricing and marketing plans for orphan medications.
  • Revolutionary changes approaching rare diseases.

Why Attend?

  • To share and exchange the recent advances and developments in rare diseases area.
  • Participate in discussions with experts on how to tackle the critical issues shaping the future of orphan drugs.
  • The best opportunity to showcase your work and research in front of industry leaders.
  • Discover and brainstorm ways to advance orphan drug development and improve access to life-saving therapies.
  • Opportunity for networking with professionals, delegates, and speakers.

Who should Attend?

Industry: Pharma/Therapeutic Companies/Start Up’s

Designations: CEOCSOCMOCOOPresidentVice PresidentDirector, Head of DepartmentExecutive LeaderSenior ManagerManagerPrinciple Scientist

Academic: Universities, Research institutes – Professors & Researchers.


  • Cell and Gene Therapy
  • Molecular Geneticist
  • Translational Science
  • Personalized & Innovative Medicine
  • External R&D Innovation
  • Regenerative Medicine
  • Rare and Ultra-Rare Diseases
  • Public, Regulatory, and Medical Affairs
  • Patient Engagement
  • Market Access
  • Patient Advocacy Groups
  • Program Management
  • Clinical Research Organizations
  • Health Economics Outcomes Research
  • Investments and Funding
  • Speciality Pharmacies

Enquire Now

Sponsor/Exhibit Delegate
Speakers will be updated soon. Please contact [email protected] for speaking opportunity
London, UK
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