Digital
15th -16th March 2022

3rd Edition MarketsandMarkets Orphan Drugs and Rare Diseases Virtual Conference [Time Zone - Central European Time (CET)]

New medicine for Orphan and Rare Diseases has the capability to undoubtedly impact the lives of patients, where historically there were few or no treatments have been provided to control the sickness. The Orphan Drug Act (ODA) established in 1983 compelled producers to expand scale to treat uncommon/orphan diseases, and the orphan drug panorama has advanced drastically. Approvals for orphan drugs has doubled in the past decade, and there are over 500 applicants in the pipeline for orphan diseases.

The 3rd Annual MarketsandMarkets Orphan Drugs and Rare Diseases Conference Virtual Event is scheduled to be held on 15th -16th March 2022 will provide valuable and necessary platform for uplifting knowledge at the forefront of drug analysis.

Over the course of the conference, internationally renowned speakers can describe how their analysis journeys have developed the response towards up-to-date challenges. The attending specialists and trade partners will offer an incredible networking expertise.

This conference will gather scientists, researchers, entrepreneurs, academicians, medical officers, CEO’s, CSO’s and technologists from everywhere around the globe to discuss on the newest scientific advances within the field of rare diseases & orphan drugs that facilitate to form current and future challenges in drug analysis.

WHAT TO EXPECT

KEY HIGHLIGHTS

  • Current Orphan Drugs landscape and implications of COVID19
  • Study worldwide patterns in uncommon infections and its advances in the remedial and demonstrative market
  • Finding innovative and alternative ways in funding the development of Orphan Drugs
  • How is FDA managing orphan drugs during the pandemic?
  • The growth of orphan drugs for rare diseases
  • Challenges and opportunities in treatment
  • Improving clinical trials for rare diseases

Who Should Attend?

Academia & CEOs, Owners, Business Heads, VPs, Directors, Heads, Managers 

From the Departments of: 

  • Personalized & Innovative Medicine
  • External R&D Innovation
  • Regenerative Medicine
  • Rare and Ultra-Rare Diseases
  • Cell and Gene Therapy
  • Molecular Geneticist
  • Translational Science
  • Patient Advocacy Groups
  • Program Management
  • Public, Regulatory, Medical   Affairs
  • Patient Engagement
  • Market Access
  • Clinical Research Organizations
  • Health Economics Outcomes Research
  • Investments and Funding
  • Business Planning and Operations
  • Specialty Pharmacies

Why attend?

  • 100+ experts attending
  • Participate in constructive discussion with leading industry experts and decision-makers from pharmaceutical manufacturers who will tackle the most important issues in Rare disease diagnosis.
  • Best opportunity to showcase your work and research in front of industry leaders.
  • Develop your skills by learning new competencies and acquire knowledge from pioneers all around the world.

CONFERENCE AGENDA
CONFERENCE SPEAKERS
Advisors
June Sanson
June Sanson
Senior Director, Patient Advocacy and Industry Relations, Acadia Pharmaceuticals Inc.
Rudiger Schulze
Rudiger Schulze
Vice President and General Manager, Germany and Central / Eastern Europe , Ultragenyx Pharmaceutical Inc.
 Dairine Dempsey
Dairine Dempsey
Non-Executive Director/Consultant, OmniSpirant Limited | Soleno Therapeutics, Inc.
Speakers
June Sanson
June Sanson
Senior Director, Patient Advocacy and Industry Relations, Acadia Pharmaceuticals Inc.
Rudiger Schulze
Rudiger Schulze
Vice President and General Manager, Germany and Central / Eastern Europe , Ultragenyx Pharmaceutical Inc.
 Dairine Dempsey
Dairine Dempsey
Non-Executive Director/Consultant, OmniSpirant Limited | Soleno Therapeutics, Inc.
Mariusz Olejniczak
Mariusz Olejniczak
Chief Executive Officer, WPD Pharmaceuticals Inc
Andreas Uttenweiler
Andreas Uttenweiler
Head of Patient Value Access & Public Affairs, Takeda Pharmaceuticals
Shailesh Agarwal
Shailesh Agarwal
Assistant Professor of Surgery, Harvard Medical School, Partner, Mainspring Venture Partners
Subir Roy
Subir Roy
Associate Director for Global Medical Affairs |Project Lead, MIT-Takeda Program on Fabry
Davy Yeung
Davy Yeung
 Managing Director and Vice President of Operations, Tailored Clinical Research Solutions (TCRS)
SPONSORS
Sponsors & Exhibitors
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TCRS (Tailored Clinical Research Solutions)

Visiting Partners
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Angelini

PAST EVENT GALLERY